In vivo selection and glymphatic delivery of AAV5 capsids engineered to target human glial progenitor cells.
体内筛选和淋巴系统递送经基因工程改造靶向人类神经胶质祖细胞的 AAV5 衣壳
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doi:10.1101/2025.07.03.662612
Cona Alexander, Newbold Evan, Kesmen Deniz, Snape Rajiv, Danner Jessica, White Nicholas, Borden William, Iseson Abigail, Schanz Steven J, Chandler-Militello Devin, Li Xiaojie, Cano Jose C, Mariani John N, Nedergaard Maiken, Benraiss Abdellatif, Goldman Steven A