日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Assessing Patient-Reported Outcomes in Acute Attacks of Hereditary Angioedema: Insights from a Mixed Methods Study of Participants Receiving Standard-of-Care Treatments in a Real-World Setting

评估遗传性血管性水肿急性发作期患者报告结局:一项在真实世界环境中接受标准治疗的参与者混合方法研究的启示

Mendivil, Joan; Zhu, Li; Bonner, Nicola; Gargon, Elizabeth; Jouvin, Marie-Helene; Abetz-Webb, Linda; Fairbanks, Hannah; Sims, Joel; Middlehurst, Jessica; Cronin, Patrick; Chen, Maggie; Cohn, Danny M; Lu, Peng; Riedl, Marc A

Association Between the Angioedema Control Test and Attack Frequency in Hereditary Angioedema

遗传性血管性水肿患者血管性水肿控制测试与发作频率之间的关联

Yarlas, Aaron; Feld, Alexandra J; Bjorner, Jakob B; Thurm, Cary; Bordone, Laura; Newman, Kenneth B; Treadwell, Sabrina; Cohn, Danny M

An International Delphi Study on Barriers to On-Demand Treatment of Hereditary Angioedema Attacks

一项关于按需治疗遗传性血管性水肿发作障碍的国际德尔菲研究

Banerji, Aleena; Aygören-Pürsün, Emel; Bara, Noemi-Anna; Bernstein, Jonathan A; Betschel, Stephen; Bouillet, Laurence; Busse, Paula J; Caballero, Teresa; Cancian, Mauro; Cohn, Danny M; Craig, Timothy; Farkas, Henriette; Grumach, Anete Sevciovic; Hide, Michihiro; Kiani-Alikhan, Sorena; Longhurst, Hilary J; Lumry, William R; Riedl, Marc A; Stobiecki, Marcin; Valerieva, Anna; Zanichelli, Andrea

Population Pharmacokinetic/Pharmacodynamic Modeling of Donidalorsen, an Antisense Oligonucleotide in Development for Prophylaxis of Hereditary Angioedema

唐尼达洛森(Donidalorsen)是一种在研的用于预防遗传性血管性水肿的反义寡核苷酸,其群体药代动力学/药效学模型研究。

Diep, John K; Liu, Miao; Singh, Pratap; Dorow, Steve; Cohn, Danny M; Bordone, Laura; Newman, Kenneth B; Gao, Xiang

Donidalorsen for Long-Term Prophylaxis of Hereditary Angioedema Attacks: Results from the OASISplus Open-Label Extension Cohort at Year 1

多尼达洛森用于遗传性血管性水肿发作的长期预防:OASISplus开放标签扩展队列第1年的结果

Lumry, William R; Tachdjian, Raffi; Craig, Timothy; Karakaya, Gül; Gelincik, Asli; Stobiecki, Marcin; Jacobs, Joshua S; Gokmen, Nihal Mete; Reshef, Avner; Manning, Michael E; Grammatikos, Alexandros; Giardino, Francesco; Guilarte, Mar; Baptist, Alan P; Bordone, Laura; Newman, Kenneth B; Treadwell, Sabrina; Lin, Tao; Yarlas, Aaron; Riedl, Marc A; Cohn, Danny M

Super refractory status epilepticus as an atypical presentation of Hashimoto's encephalopathy

超难治性癫痫持续状态是桥本脑病的一种非典型表现

Chaponan-Lavalle, Andres; Alave, Jorge; Fernandez, Fred; Hermoza, Luciana Chacon; Barrientos-Iman, Danny M; Chulluncuy-Rivas, Roberto; Diaz, Nelson

Patient-Reported Outcomes in the Phase III OASIS-HAE Study of Donidalorsen for Hereditary Angioedema

多尼达洛森治疗遗传性血管性水肿的III期OASIS-HAE研究中的患者报告结局

Riedl, Marc A; Yarlas, Aaron; Bordone, Laura; Treadwell, Sabrina; Wang, Sophie; Newman, Kenneth B; Cohn, Danny M

Hereditary Angioedema with Normal C1 Inhibitor: an Updated International Consensus Paper on Diagnosis, Pathophysiology, and Treatment

遗传性血管性水肿伴正常C1抑制剂:诊断、病理生理学和治疗的最新国际共识文件

Zuraw, Bruce L; Bork, Konrad; Bouillet, Laurence; Christiansen, Sandra C; Farkas, Henriette; Germenis, Anastasios E; Grumach, Anete S; Kaplan, Allen; López-Lera, Alberto; Magerl, Markus; Riedl, Marc A; Adatia, Adil; Banerji, Aleena; Betschel, Stephen; Boccon-Gibod, Isabelle; Bova, Maria; Boysen, Henrik Balle; Caballero, Teresa; Cancian, Mauro; Castaldo, Anthony J; Cohn, Danny M; Corcoran, Deborah; Drouet, Christian; Fukunaga, Atsushi; Hide, Michihiro; Katelaris, Constance H; Li, Philip H; Longhurst, Hilary; Peter, Jonny; Psarros, Fotis; Reshef, Avner; Ritchie, Bruce; Selva, Christine N; Zanichelli, Andrea; Maurer, Marcus

Expert Strategies: Skull Base Reconstruction-Global Perspectives, Insights, and Algorithms through a Mixed Methods Approach

专家策略:颅底重建——基于混合方法论的全球视角、见解和算法

Kuan, Edward C; Talati, Vidit; Patel, Jagatkumar A; Nguyen, Theodore V; Abiri, Arash; Pang, Jonathan C; Goshtasbi, Khodayar; Liu, Lauren; Craig, John R; Papagiannopoulos, Peter; Phillips, Katie M; Tajudeen, Bobby A; Adappa, Nithin D; Palmer, James N; Sedaghat, Ahmad R; Wang, Eric W; Anand, Vijay; Batra, Pete S; Bergsneider, Marvin; Bernal-Sprekelsen, Manuel; Bleier, Benjamin S; Cappabianca, Paolo; Carrau, Ricardo L; Casiano, Roy R; Castelnuovo, Paolo; Cavallo, Luigi M; Cohen, Marc A; Dallan, Iacopo; Eloy, Jean Anderson; El-Sayed, Ivan H; Evans, James J; Fernandez-Miranda, Juan C; Ferrari, Marco; Froelich, Sebastien; Gardner, Paul A; Georgalas, Christos; Gray, Stacey T; Hanna, Ehab Y; Harvey, Richard J; Hong, Sang Duk; Hwang, Peter H; Kelly, Daniel F; Kong, Doo-Sik; Lan, Ming-Ying; Lee, John Y K; Levine, Corinna G; Liu, James K; Locatelli, Davide; Meço, Cem; McKean, Erin L; Nicolai, Piero; Nyquist, Gurston G; Omura, Kazuhiro; Passeri, Thibault; Patel, Zara M; Celda, Maria Peris; Neto, Carlos Pinheiro; Prevedello, Danny M; Rabinowitz, Mindy R; Raza, Shaan M; Recinos, Pablo F; Rosen, Marc R; Sargi, Zoukaa B; Schlosser, Rodney J; Schwartz, Theodore H; Sindwani, Raj; Snyderman, Carl H; Stamm, Aldo C; Thorp, Brian D; Turri-Zanoni, Mario; Wang, Marilene B; Wang, Wei-Hsin; Witterick, Ian J; Won, Tae-Bin; Woodworth, Bradford A; Wormald, Peter-John; Zada, Gabriel; Su, Shirley Y

A sensitive and specific assay to characterize plasma kallikrein activity in plasma from patients with hereditary angioedema

一种灵敏且特异的检测方法,用于表征遗传性血管性水肿患者血浆中的激肽释放酶活性。

Lee, Daniel K; Ghannam, Arije; Murugesan, Nivetha; Vincent, Denis; Dona, Micaela; Cohn, Danny M; Adatia, Adil; Smith, Michael D; Audhya, Paul K; Hampton, Sally L; Feener, Edward P