日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Deep evolutionary conservation of a sex-determining locus without sequence homology

性别决定基因位点在无序列同源性的情况下表现出深层的进化保守性

Yu, Chuanxin; Hodapp, Dean; Moog, Safira; Dupont, Simon; Darrouzet, Eric; Keller Valsecchi, Claudia Isabelle; Colgan, Thomas Joseph; Pan, Qiaowei; Darras, Hugo

Data from long-term experiments in temperate croplands to evaluate soil organic carbon models

利用温带农田长期试验数据评估土壤有机碳模型

Fujisaki, Kenji; Ferchaud, Fabien; Clivot, Hugues; Bruni, Elisa; Guenet, Bertrand; Pichot, Christian; Versini, Antoine; Baudin, François; Bispo, Antonio; Peylin, Philippe; Martin, Manuel P; Jensen, Johannes L; Eriksen, Jørgen; Chenu, Claire; Gregory, Andrew S; Glendining, Margaret J; Merbach, Ines; Beaudoin, Nicolas; Mary, Bruno; Mollier, Alain; Tison, Gilles; Montagnier, Christophe; Chabbi, Abad; Vertès, Françoise; Cadéro, Alice; Graux, Anne-Isabelle; Pellerin, Sylvain; Levavasseur, Florent; Gilles, Manon; Morvan, Thierry; Resseguier, Camille; Milesi, Luis; Irizar, Alicia; Andriulo, Adriàn; Mistou, Marie-Noël; Butier, Arnaud; Bertrand, Michel; Autret, Bénédicte; Jeuffroy, Marie-Hélène; Grandeau, Gilles; Doré, Thierry; Cellier, Vincent; Berthier, Alain; Darras, Sébastien; Audebert, Guillaume; Pasquier, Ludovic; Ecalle, Fabien; Savoie, Antoine; Schiedung, Marcus; Poeplau, Christopher; Maaroufi, Nadia I; Kätterer, Thomas; Bolinder, Martin A; Sanderman, Jonathan; Barré, Pierre

Liver Steatosis in Induced Hepatocytes From Carriers of Spinal Muscular Atrophy

脊髓性肌萎缩症携带者诱导肝细胞的肝脂肪变性

Sun, Lingyu; Leow, Damien Meng Kiat; Wang, Loo Chien; Eio, Michelle Yating; Koh, Hiromi W L; Khong, Zi Jian; Narayanan, Gunaseelan; Teo, Aloysius Kai Soon; Giadone, Richard; Sobota, Radoslaw M; Ng, Shi Yan; Teo, Adrian Kee Keong; Ong, Wei Yi; Rubin, Lee L; Darras, Basil T; Yeo, Crystal J J

Impact of an early warning system on the outcome of patients with haematological malignancies receiving high-dose chemotherapy with or without haematopoietic cell transplantation: a protocol of the ALHERT cluster randomised trial

早期预警系统对接受大剂量化疗(伴或不伴造血干细胞移植)的血液系统恶性肿瘤患者预后的影响:ALHERT整群随机试验方案

Taillantou-Candau, Mathilde; Kouatchet, Achille; Darsonval, Astrid; Monmousseau, Fanny; Darras, Elise; Schmidt, Aline; Riou, Jérémie; Orvain, Corentin

WABAD: A world annotated bird acoustic dataset for passive acoustic monitoring

WABAD:一个用于被动声学监测的全球鸟类声学标注数据集

Pérez-Granados, Cristian; Morant, Jon; Darras, Kevin F A; Marín-Gómez, Oscar H; Mendoza, Irene; Muñoz-Mohedano, Miguel A; Santamaría-García, Eduardo; Bastianelli, Giulia; Márquez-Rodríguez, Alba; Budka, Michał; Bota, Gerard; De la Peña-Rubio, José M; de la Morena, Eladio L García; Santa-Cruz, Manu; de la Nava, Pablo; Fernández-Tizón, Mario; Sánchez-Mateos, Hugo; Barrero, Adrián; Traba, Juan; Osiejuk, Tomasz S; Hart, Patrick J; Navine, Amanda K; Montoya Muñoz, Andrés F; de Araujo, Carlos B; Rosa, Gabriel L M; Denóbile Torres, Ingrid M; Camargo Catalano, Ana L; Simões, Cássio Rachid; Llusia, Diego; Morales, Manuel B; Acebes, Pablo; Medina, Juan A; Brown, Nicholas; Astaras, Christos; Karmiris, Ilias; Navarrete, Elizabeth; Cauchoix, Maxime; Barbaro, Luc; Funosas, David; Arend, Dominik; Müeller, Sandra; González-García, Fernando; González-Romero, Alberto; Mammides, Christos; Pontikis, Michaelangelo; Jacuzzi, Giordano; Olden, Julian D; Bombaci, Sara P; Marcacci, Gabriel; Jacot, Alain; Zurano, Juan P; Gangenova, Elena; Varela, Diego; Di Sallo, Facundo; Zurita, Gustavo A; Atemasov, Andrey; Tremblay, Junior A; Lamarre, Vincent; Hutschenreiter, Anja; Monroy-Ojeda, Alan; Díaz-Vallejo, Mauricio; Chaparro-Herrera, Sergio; Briers, Robert A; Sousa-Lima, Renata; Pinheiro, Thiago; da Silva, Wigna C; Calvente, Alice; Molin, Anamaria Dal; Antonelli, Alexandre; Gogoleva, Svetlana; Palko, Igo; Trọng, Hiếu Vũ; Lage Duarte, Marina H; Dos Santos Saturnino, Natalia; Silva, Samuel R; Rainho, Ana; Lopes, Paula; Schuchmann, Karl-L; Marques, Marinêz I; de Oliveira, Ana S; Littlewood, Nick A; Tuanmu, Mao-Ning; Cheng, Yi-Ru; Chao, Hsuan; Kepfer-Rojas, Sebastian; Aguilera, Andrea L; Brotons, Lluís; Feldman, Mariano J; Imbeau, Louis; Panwar, Pooja; Weed, Aaron S; Deshwal, Anant; da Paz, Raiane Vital; Salustio-Gomes, Carlos; Oliveira-Júnior, Dorgival D; Lima-Santos, Cicero S; Pichorim, Mauro; Pan, Wuyuan; Goodale, Eben; Attisano, Alfredo; Theuerkauf, Jörn; Sebastián-González, Esther

Software Tools for Passive Acoustic Monitoring in Aquatic and Terrestrial Bio- and Ecoacoustics: A Living Systematic Review

用于水生和陆生生物及生态声学被动声学监测的软件工具:动态系统综述

Hanf-Dressler, Tara; Nouioua, Rym; Thomisch, Karolin; Cazau, Dorian; de Selys Longchamps, Simon; Darras, Kevin F A

Analysis of human urinary extracellular vesicles reveals disordered renal metabolism in myotonic dystrophy type 1

对人类尿液细胞外囊泡的分析揭示了1型强直性肌营养不良症患者的肾脏代谢紊乱

Preeti Kumari,Lauren M Sullivan,Zhaozhi Li,E Parker Conquest,Elizabeth Cornforth,Rojashree Jayakumar,Ningyan Hu,J Alexander Sizemore,Brigham B McKee,Robert R Kitchen,Paloma González-Pérez,Constance Linville,Karla Castro,Hilda Gutierrez,Soleil Samaan,Elise L Townsend,Basil T Darras,Seward B Rutkove,Susan T Iannaccone,Paula R Clemens,Araya Puwanant,Sudeshna Das,Thurman M Wheeler

Spinal Muscular Atrophy Functional Composite Score Revised (SMA-FCR) in Untreated and Nusinersen-Treated Patient Cohorts

脊髓性肌萎缩症功能综合评分修订版(SMA-FCR)在未治疗和接受Nusinersen治疗的患者队列中的比较

Pasternak, Amy; McDermott, Michael P; Montes, Jacqueline; Glanzman, Allan M; Coratti, Giorgia; Dunaway Young, Sally; Duong, Trinh Tina; Martens, William B; Day, John W; Zolkipli-Cunningham, Zarazuela; Sansone, Valeria Ada; D'Amico, Adele; Messina, Sonia; Bruno, Claudio; Mercuri, Eugenio; De Vivo, Darryl C; Darras, Basil T