SINEUP RNA rescues molecular phenotypes associated with CHD8 suppression in autism spectrum disorder model systems.
SINEUP RNA 可挽救自闭症谱系障碍模型系统中与 CHD8 抑制相关的分子表型
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.12.043
Di Leva Francesca, Arnoldi Michele, Santarelli Stefania, Massonot Mathieu, Lemée Marianne Victoria, Bon Carlotta, Pellegrini Miguel, Castellini Maria Elena, Zarantonello Giulia, Messina Andrea, Bozzi Yuri, Bernier Raphael, Zucchelli Silvia, Casarosa Simona, Dassi Erik, Ronzitti Giuseppe, Golzio Christelle, Morandell Jasmin, Gustincich Stefano, Espinoza Stefano, Biagioli Marta