Framework for Multistakeholder Patient Registries in the Field of Rare Diseases: Focus on Neurogenetic Diseases
罕见病领域多方利益相关者患者登记框架:聚焦神经遗传疾病
期刊:Neurology
影响因子:8.5
doi:10.1212/WNL.0000000000209743
Schoenmakers, Daphne H; van den Berg, Sibren; Timmers, Lonneke; Adang, Laura A; Bäumer, Tobias; Bosch, Annet; van de Casteele, Marc; Datema, Mareen R; Dekker, Hanka; Donnelly, Conan; Driessens, Mariëtte H E; Graessner, Holm; Greger, Valerie; Haddad, Tala; Höglinger, Günter U; van den Hout, Hannerieke; Jonker, Carla; Langeveld, Mirjam; Lambert, Laurie J; Neacy, Eileen; Nieuwland, Marc; Klockgether, Thomas; van der Knaap, Marjo S; Papadopoulou, Andri; Plueschke, Kelly; van Rijn, Sanne; Rosenberg, Noa; Saunier-Vivar, Elise F; Dos Santos Vieira, Bruna; Hollak, Carla E M; Goettsch, Wim G; Wolf, Nicole I