日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficient in vivo genome editing prevents hypertrophic cardiomyopathy in mice

有效的体内基因组编辑可预防小鼠肥厚性心肌病

Daniel Reichart #, Gregory A Newby #, Hiroko Wakimoto #, Mingyue Lun, Joshua M Gorham, Justin J Curran, Aditya Raguram, Daniel M DeLaughter, David A Conner, Júlia D C Marsiglia, Sajeev Kohli, Lukas Chmatal, David C Page, Nerea Zabaleta, Luk Vandenberghe, David R Liu, Jonathan G Seidman, Christine Se

Ablation of lysophosphatidic acid receptor 1 attenuates hypertrophic cardiomyopathy in a mouse model

溶血磷脂酸受体 1 的消融可减轻小鼠模型中的肥厚性心肌病

Anna Axelsson Raja, Hiroko Wakimoto, Daniel M DeLaughter, Daniel Reichart, Joshua Gorham, David A Conner, Mingyue Lun, Clemens K Probst, Norihiko Sakai, Rachel S Knipe, Sydney B Montesi, Barry Shea, Leonard P Adam, Leslie A Leinwand, William Wan, Esther Sue Choi, Eric L Lindberg, Giannino Patone, Mi

BET bromodomain proteins regulate transcriptional reprogramming in genetic dilated cardiomyopathy

BET 溴结构域蛋白调节遗传性扩张型心肌病的转录重编程

Andrew Antolic, Hiroko Wakimoto, Zhe Jiao, Joshua M Gorham, Steven R DePalma, Madeleine E Lemieux, David A Conner, Da Young Lee, Jun Qi, Jonathan G Seidman, James E Bradner, Jonathan D Brown, Saptarsi M Haldar, Christine E Seidman, Michael A Burke

CRISPR/Cas9-Mediated Fluorescent Tagging of Endogenous Proteins in Human Pluripotent Stem Cells

CRISPR/Cas9 介导的人类多能干细胞内源性蛋白质的荧光标记

Arun Sharma, Christopher N Toepfer, Tarsha Ward, Lauren Wasson, Radhika Agarwal, David A Conner, Johnny H Hu, Christine E Seidman

Surfactant protein-C chromatin-bound green fluorescence protein reporter mice reveal heterogeneity of surfactant protein C-expressing lung cells

表面活性蛋白 C 染色质结合绿色荧光蛋白报告小鼠揭示表面活性蛋白 C 表达肺细胞的异质性

Joo-Hyeon Lee, Jonghwan Kim, David Gludish, Rebecca R Roach, Arven H Saunders, Juliana Barrios, Andrew Jonghan Woo, Huaiyong Chen, David A Conner, Yuko Fujiwara, Barry R Stripp, Carla F Kim