Mutant allele knockout with novel CRISPR nuclease promotes myelopoiesis in ELANE neutropenia
利用新型 CRISPR 核酸酶敲除突变等位基因可促进 ELANE 中性粒细胞减少症中的骨髓细胞生成
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2022.06.002
Peter Sabo, Vahagn Makaryan, Yosef Dicken, Lital Povodovski, Liat Rockah, Tzlil Bar, Matan Gabay, Dalia Elinger, Ella Segal, Ora Haimov, Maya Antoshvili, Anat London Drori, Tanoya Poulsen, Asael Herman, Rafi Emmanuel, David C Dale