An Investigational RNAi Therapeutic Targeting Glycolate Oxidase Reduces Oxalate Production in Models of Primary Hyperoxaluria
针对乙醇酸氧化酶的在研 RNAi 疗法可减少原发性高草酸尿症模型中的草酸生成
期刊:Journal of the American Society of Nephrology
影响因子:10.3
doi:10.1681/ASN.2016030338
Abigail Liebow, Xingsheng Li, Timothy Racie, Julia Hettinger, Brian R Bettencourt, Nader Najafian, Patrick Haslett, Kevin Fitzgerald, Ross P Holmes, David Erbe, William Querbes, John Knight