Human, economic, and social impact of lysosomal storage diseases
溶酶体贮积症对人类、经济和社会的影响
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-04053-z
Brignani, Eduardo; de Castro-López, María José; Gonzalez-Meneses, Antonio; Morales, Montserrat; Pintos-Morell, Guillem; Poveda, José Luis; Vilalta, Imma; Cruz, Jordi; Ballester-Lozano, Gabriel Fernando; David de Paz, Héctor