Messenger RNA rescues medium-chain acyl-CoA dehydrogenase deficiency in fibroblasts from patients and a murine model
信使RNA可挽救患者和鼠模型成纤维细胞中的中链酰基辅酶A脱氢酶缺乏症
期刊:Human Molecular Genetics
影响因子:3.2
doi:10.1093/hmg/ddad076
Zhao, Xue-Jun; Mohsen, Ai-Walid; Mihalik, Stephanie; Solo, Keaton; Basu, Shakuntala; Aliu, Ermal; Shi, Huifang; Kochersberger, Catherine; Karunanidhi, Anuradha; Van't Land, Clinton; Coughlan, Kimberly A; Siddiqui, Summar; Rice, Lisa M; Hillier, Shawn; Guadagnin, Eleonora; DeAntonis, Christine; Giangrande, Paloma H; Martini, Paolo G V; Vockley, Jerry
