Functional benefit of CRISPR-Cas9-induced allele deletion for RYR1 dominant mutation
CRISPR-Cas9诱导的等位基因缺失对RYR1显性突变的功能益处
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2024.102259
Beaufils, Mathilde; Melka, Margaux; Brocard, Julie; Benoit, Clement; Debbah, Nagi; Mamchaoui, Kamel; Romero, Norma B; Dalmas-Laurent, Anne Frédérique; Quijano-Roy, Susana; Fauré, Julien; Rendu, John; Marty, Isabelle