Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV
使用外泌体相关 AAV 将基因传递至内耳毛细胞以挽救听力
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2016.12.010
Bence György, Cyrille Sage, Artur A Indzhykulian, Deborah I Scheffer, Alain R Brisson, Sisareuth Tan, Xudong Wu, Adrienn Volak, Dakai Mu, Panos I Tamvakologos, Yaqiao Li, Zachary Fitzpatrick, Maria Ericsson, Xandra O Breakefield, David P Corey, Casey A Maguire