An AAVS1-targeted minigene platform for correction of iPSCs from all five types of chronic granulomatous disease
针对 AAVS1 的微基因平台，用于矫正所有五种慢性肉芽肿性疾病的 iPSC
期刊:Molecular Therapy
影响因子:12.1
doi:10.1038/mt.2014.195
Randall K Merling, Colin L Sweeney, Jessica Chu, Aaron Bodansky, Uimook Choi, Debra Long Priel, Douglas B Kuhns, Hongmei Wang, Sam Vasilevsky, Suk See De Ravin, Thomas Winkler, Cynthia E Dunbar, Jizhong Zou, Kol A Zarember, John I Gallin, Steven M Holland, Harry L Malech
