In utero CRISPR-mediated therapeutic editing of metabolic genes
利用 CRISPR 介导的子宫内代谢基因治疗性编辑
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-018-0184-6
Avery C Rossidis # ,John D Stratigis # ,Alexandra C Chadwick # ,Heather A Hartman # ,Nicholas J Ahn ,Haiying Li ,Kshitiz Singh ,Barbara E Coons ,Li Li ,Wenjian Lv ,Philip W Zoltick ,Deepthi Alapati ,William Zacharias ,Rajan Jain ,Edward E Morrisey ,Kiran Musunuru ,William H Peranteau