日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Prime Editing Modification with FEN1 Improves F508del Variant Editing in the CFTR Gene in Airway Basal Cells.

利用 FEN1 进行 Prime Editing Modification 可改善气道基底细胞中 CFTR 基因的 F508del 变异体编辑

Volodina Olga V, Demchenko Anna G, Anuchina Arina A, Ryzhkova Oxana P, Kovalskaya Valeriia A, Kondrateva Ekaterina V, Artemova Ekaterina V, Tabakov Vyacheslav Y, Ignatov Maxim A, Vorobyeva Natalia Y, Osipov Andreyan N, Lavrov Alexander V, Smirnikhina Svetlana A

CFAP300 Loss-of-Function Mutations with Primary Ciliary Dyskinesia: Evidence from Ex Vivo and ALI Cultures.

CFAP300 功能丧失突变与原发性纤毛运动障碍:来自体外和 ALI 培养的证据

Demchenko Anna G, Kyian Tatiana A, Kondratyeva Elena I, Bragina Elizaveta E, Ryzhkova Oksana P, Veiko Roman V, Nazarova Aleksandra G, Chernykh Vyacheslav B, Smirnikhina Svetlana A, Kutsev Sergey I