日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Combination of a TGF-β ligand trap (RAP-GRL) and TMPRSS6-ASO is superior for correcting β-thalassemia.

TGF-β配体陷阱(RAP-GRL)与TMPRSS6-ASO的组合在纠正β-地中海贫血方面更胜一筹

Guerra Amaliris, Hamilton Nolan, Rivera Ariel, Demsko Perry, Guo Shuling, Rivella Stefano

S101: COMBINATION OF A LUSPATERCEPT-LIKE DRUG (RAP-GRL) AND TMPRSS6-ASO IS SUPERIOR TO EITHER DRUG ALONE FOR CORRECTING β-THALASSEMIA

S101:LUSPATERCEPT 样药物 (RAP-GRL) 与 TMPRSS6-ASO 联合用药在纠正 β-地中海贫血方面优于单独使用任何一种药物

Trojani, Alessandra; Montillo, Marco; Nichelatti, Michele; Tedeschi, Alessandra; Colombo, Chiara; Veronese, Silvio; Mura, Maria Angela; Ricci, Francesca; Scarpati, Barbara; Colosimo, Anna; Lodola, Milena; Morra, Enrica; Agrippa, OA; Summers, KZ; Anie, KA; Telfer, P; Lugthart, S; De La Fuente, A; Peñalver, F J; Herrera, P; Cordoba, R; Martinez Chamorro, C; Olave, M T; Jarque, I; Navarro, M B; Estévez, M; Masarova, L; Bose, P; Pemmaraju, N; Chifotides, H; Zhou, L; Estrov, Z; Kantarjian, H; Verstovsek, S; Sgherza, N; Curci, P; Rizzi, R; Roccotelli, D; Croce, M; Avantaggiato, M; Ruga, L; Vitucci, A; Palma, A; Di Gennaro, D; Musto, P; Sgherza, N; Rizzi, R; Curci, P; Roccotelli, D; Croce, M; Avantaggiato, M; Ruga, L; Musto, P; Guerra, A; Demsko, P; Sinha, S; McVeigh, P; Castruccio Castracani, C; Breda, L; Casu, C; Rivella, S