Adeno-associated virus-mediated CASQ2 delivery rescues phenotypic alterations in a patient-specific model of recessive catecholaminergic polymorphic ventricular tachycardia.
腺相关病毒介导的 CASQ2 递送可挽救隐性儿茶酚胺能多形性室性心动过速患者特异性模型中的表型改变
期刊:Cell Death & Disease
影响因子:9.6
doi:10.1038/cddis.2016.304
Lodola Francesco, Morone Diego, Denegri Marco, Bongianino Rossana, Nakahama Hiroko, Rutigliano Lucia, Gosetti Rosanna, Rizzo Giulia, Vollero Alessandra, Buonocore Michelangelo, Napolitano Carlo, Condorelli Gianluigi, Priori Silvia G, Di Pasquale Elisa