Volumetric MRI of dorsal root ganglia as a biomarker for disease progression and response to AAV treatment in a mouse model of Fabry disease.
在法布里病小鼠模型中,背根神经节的体积磁共振成像可作为疾病进展和对 AAV 治疗反应的生物标志物。
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0334840
Zhao Fuqiang, Yuan Shipeng, Kaittanis Charalambos, Deshpande Mugdha, Kugadas Abirami, Derakhchan Katayoun, Ruangsiriluk Wanida, Islam Rizwana, Boukharov Natalia, McQuade Paul, Tauscher Johannes, Winkelmann Christopher T, Lohith Talakad G