Short antisense oligonucleotides alleviate the pleiotropic toxicity of RNA harboring expanded CGG repeats
短反义寡核苷酸可减轻含有扩增 CGG 重复序列的 RNA 的多效性毒性
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-021-21021-w
Magdalena Derbis, Emre Kul, Daria Niewiadomska, Michał Sekrecki, Agnieszka Piasecka, Katarzyna Taylor, Renate K Hukema, Oliver Stork, Krzysztof Sobczak