The von Willebrand factor-binding aptamer rondaptivon pegol as a treatment for severe and nonsevere hemophilia A
血管性血友病因子结合适体rondaptivon pegol可作为治疗重度和非重度A型血友病的药物
期刊:Blood
影响因子:23.1
doi:10.1182/blood.2022016571
Ay, Cihan; Kovacevic, Katarina D; Kraemmer, Daniel; Schoergenhofer, Christian; Gelbenegger, Georg; Firbas, Christa; Quehenberger, Peter; Jilma-Stohlawetz, Petra; Gilbert, James C; Zhu, Shuhao; Beliveau, Martin; Koenig, Franz; Iorio, Alfonso; Jilma, Bernd; Derhaschnig, Ulla; Pabinger, Ingrid