Velaglucerase alfa (VPRIV) enzyme replacement therapy in patients with Gaucher disease: Long-term data from phase III clinical trials
戈谢病患者接受维拉葡糖苷酶α (VPRIV) 酶替代疗法:来自 III 期临床试验的长期数据
期刊:American Journal of Hematology
影响因子:9.9
doi:10.1002/ajh.24012
Hughes, Derralynn A; Gonzalez, Derlis E; Lukina, Elena A; Mehta, Atul; Kabra, Madhulika; Elstein, Deborah; Kisinovsky, Isaac; Giraldo, Pilar; Bavdekar, Ashish; Hangartner, Thomas N; Wang, Nan; Crombez, Eric; Zimran, Ari