日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Longitudinal imaging of therapeutic enzyme expression after gene therapy for Fabry disease using positron emission tomography and the radiotracer [(18)F]AGAL

利用正电子发射断层扫描和放射性示踪剂[(18)F]AGAL对法布里病基因治疗后治疗性酶的表达进行纵向成像

Kaittanis, Charalambos; Teceno, Tyler; Knight, Ashley; Petibon, Yoann; Sandoval, Phil; Cohen, Lawrence; Ahn, Shin Hye; Belanger, Anthony P; Clark, Louise M; Nguyen, Quang-De; Ruangsiriluk, Wanida; Mukherji, Shreya; Constantinescu, Cristian C; Amenta, Amy Llopis; Narayanan, Sarav; Deshpande, Mugdha; Islam, Rizwana; Yuan, Shipeng; McQuade, Paul; Winkelmann, Christopher T; Lohith, Talakad G

Biodistribution of AAV1, AAV5, AAV9, and AAVDJ serotypes after intra-cisterna magna delivery in non-human primates

非人灵长类动物经枕大池内给药后AAV1、AAV5、AAV9和AAVDJ血清型的生物分布

Okai, Takuro; Sato, Sho; Yasuno, Hironobu; Nakayama, Miyu; Yamamoto, Syunsuke; Sjöqvist, Sebastian; Otake, Kentaro; Nakashima, Masato; Deshpande, Mugdha; Galbreath, Elizabeth; Oak, Jeong-Ho; Miyamoto, Saku; Proetzel, Gabriele

Paramagnetic rim lesions are highly specific for multiple sclerosis in real-world data

真实世界数据显示,顺磁性环状病变对多发性硬化症具有高度特异性。

Hemond, Christopher C; Dundamadappa, Sathish K; Deshpande, Mugdha; Baek, Jonggyu; Brown, Robert H Jr; Ionete, Carolina; Reich, Daniel S

Reversing Pathology in an Aggravated Fabry Mouse Model Using Low-Dose Engineered Human Alpha-Galactosidase A AAV Gene Therapy.

利用低剂量工程化人α-半乳糖苷酶A AAV基因疗法逆转加重型法布里病小鼠模型的病理变化

Ruangsiriluk Wanida, Deshpande Mugdha, Boukharov Natalia, Rajarshi Girija, Mukherji Shreya, Yuan Shipeng, Wiseman Jennifer, Chen Nancy, Park Eric, Cho Hyelim, Islam Rizwana

Predictors of gestational weight gain in western India: Findings from a longitudinal study across rural and urban cohorts

印度西部地区妊娠期体重增加的预测因素:一项涵盖农村和城市人群的纵向研究结果

Deshpande, Mugdha; Kajale, Neha; Shah, Nikhil; Gondhalekar, Ketan; Patwardhan, Vivek; Raiturker, Anagha Pai; Gupte, Sanjay; Patankar, Leena; Bhawra, Jasmin; Khadilkar, Anuradha; Katapally, Tarun Reddy

Volumetric MRI of dorsal root ganglia as a biomarker for disease progression and response to AAV treatment in a mouse model of Fabry disease.

在法布里病小鼠模型中,背根神经节的体积磁共振成像可作为疾病进展和对 AAV 治疗反应的生物标志物。

Zhao Fuqiang, Yuan Shipeng, Kaittanis Charalambos, Deshpande Mugdha, Kugadas Abirami, Derakhchan Katayoun, Ruangsiriluk Wanida, Islam Rizwana, Boukharov Natalia, McQuade Paul, Tauscher Johannes, Winkelmann Christopher T, Lohith Talakad G

AAV delivery of GBA1 suppresses α-synuclein accumulation in Parkinson's disease models and restores functions in Gaucher's disease models.

AAV递送GBA1可抑制帕金森病模型中α-突触核蛋白的积累,并恢复戈谢病模型中的功能

Okai Takuro, Sato Sho, Deshpande Mugdha, Matsumoto Shin-Ichi, Nakayama Miyu, Yamamoto Syunsuke, Strack-Logue Bettina, Hioki Takeshi, Tanaka Maiko, Proetzel Gabriele

Longitudinal insights into maternal body composition across trimesters of pregnancy

对孕期三个阶段母体身体成分的纵向研究

Deshpande, Mugdha; Kajale, Neha; Shah, Nikhil; Gondhalekar, Ketan; Patwardhan, Vivek; Raiturker, Anagha Pai; Gupte, Sanjay; Patankar, Leena; Khadilkar, Anuradha

A single-arm, open-label pilot study of neuroimaging, behavioral, and peripheral inflammatory correlates of mindfulness-based stress reduction in multiple sclerosis

一项单臂、开放标签的试点研究,旨在探讨基于正念的压力缓解疗法对多发性硬化症患者的神经影像学、行为学和外周炎症的相关性。

Hemond, Christopher C; Deshpande, Mugdha; Berrios-Morales, Idanis; Zheng, Shaokuan; Meyer, Jerrold S; Slavich, George M; Cole, Steven W

Targeted proteomics of cerebrospinal fluid in treatment naïve multiple sclerosis patients identifies immune biomarkers of clinical phenotypes

对未经治疗的多发性硬化症患者脑脊液进行靶向蛋白质组学分析,可识别临床表型的免疫生物标志物

Rabin, Alexandra; Bello, Elisa; Kumar, Saurabh; Zeki, Dalia Abou; Afshari, Khashayar; Deshpande, Mugdha; Francis, Nimmy; Khalighinejad, Farnaz; Umeton, Raffaella; Radu, Irina; Qutab, Fatima; Kwong, Danny; Kurban, Mariana; Hemond, Christopher; Richmond, Jillian M; Ionete, Carolina