日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Crossing the finish line towards a disease-modifying treatment for Angelman syndrome

距离研发出安格曼综合征的疾病改善疗法又近了一步

Judson, Matthew C; de Almeida, Luis Pereira; Burdine, Rebecca D; Chamberlain, Stormy J; Deverman, Benjamin E; Distel, Ben; Ehlers, Michael D; Jalazo, Elizabeth; Kushner, Steven A; Nespeca, Mark; Sanders, Stephan J; Scheffner, Martin; Yi, Jason J; Zylka, Mark J; Elgersma, Ype; Philpot, Benjamin D

Author Correction: In vivo base editing extends lifespan of a humanized mouse model of prion disease

作者更正:体内碱基编辑延长了朊病毒病人源化小鼠模型的寿命

An, Meirui; Davis, Jessie R; Levy, Jonathan M; Serack, Fiona E; Harvey, John W; Brauer, Pamela P; Pirtle, Catherine P; Berríos, Kiara N; Newby, Gregory A; Yeh, Wei-Hsi; Kamath, Nikita; Mortberg, Meredith; Lian, Yuan; Howard, Michael; DeSouza-Lenz, Kendrick; Guzman, Kenia; Thai, Aaron; Graffam, Samantha; Laversenne, Vanessa; Coffey, Alissa A; Frei, Jeannine; Pierce, Sarah E; Safar, Jiri G; Deverman, Benjamin E; Minikel, Eric Vallabh; Vallabh, Sonia M; Liu, David R

In vivo base editing extends lifespan of a humanized mouse model of prion disease.

体内碱基编辑延长了朊病毒疾病人源化小鼠模型的寿命

An Meirui, Davis Jessie R, Levy Jonathan M, Serack Fiona E, Harvey John W, Brauer Pamela P, Pirtle Catherine P, Berríos Kiara N, Newby Gregory A, Yeh Wei-Hsi, Kamath Nikita, Mortberg Meredith, Lian Yuan, Howard Michael, DeSouza-Lenz Kendrick, Guzman Kenia, Thai Aaron, Graffam Samantha, Laversenne Vanessa, Coffey Alissa A, Frei Jeannine, Pierce Sarah E, Safar Jiri G, Deverman Benjamin E, Minikel Eric Vallabh, Vallabh Sonia M, Liu David R

Brain endothelial gap junction coupling enables rapid vasodilation propagation during neurovascular coupling.

脑内皮细胞间隙连接耦合能够促进神经血管耦合过程中血管舒张的快速传播

Krolak Trevor, Kaplan Luke, Navas Kathleen, Chen Lujing, Birmingham Austin, Ryvkin Daniel, Izsa Victoria, Powell Megan, Wu Zhuhao, Deverman Benjamin E, Gu Chenghua

Cell-surface proteomic profiling identifies CD72 as a regulator of microglial tiling.

细胞表面蛋白质组学分析表明 CD72 是小胶质细胞铺展的调节因子

Chan Tamara C, Rastogi Mohit, Williams Micah X, Zhang Samuel, Shi Sophia M, Shuken Steven R, Bartling Teresa, Wild Katleen, Atkins Micaiah, Hahn Oliver, Paulo Joao A, Jereb Saša, Shuster S Andrew, Yoo Yongjin, Napole Alan, Hernandez Victoria G, Luo Liqun, Buckwalter Marion S, Stevens Beth, Deverman Benjamin E, Kronenberg-Versteeg Deborah, Gygi Steven P, Wyss-Coray Tony, Wernig Marius

Publisher Correction: Spatial atlas of the mouse central nervous system at molecular resolution

出版商更正:小鼠中枢神经系统分子分辨率空间图谱

Shi, Hailing; He, Yichun; Zhou, Yiming; Huang, Jiahao; Maher, Kamal; Wang, Brandon; Tang, Zefang; Luo, Shuchen; Tan, Peng; Wu, Morgan; Lin, Zuwan; Ren, Jingyi; Thapa, Yaman; Tang, Xin; Chan, Ken Y; Deverman, Benjamin E; Shen, Hao; Liu, Albert; Liu, Jia; Wang, Xiao

Brainwide silencing of prion protein by AAV-mediated delivery of an engineered compact epigenetic editor

通过腺相关病毒(AAV)介导递送工程化紧凑型表观遗传编辑器,实现全脑朊病毒蛋白的沉默。

Edwin N Neumann # ,Tessa M Bertozzi # ,Elaine Wu ,Fiona Serack ,John W Harvey ,Pamela P Brauer ,Catherine P Pirtle ,Alissa Coffey ,Michael Howard ,Nikita Kamath ,Kenney Lenz ,Kenia Guzman ,Michael H Raymond ,Ahmad S Khalil ,Benjamin E Deverman ,Eric Vallabh Minikel ,Sonia M Vallabh ,Jonathan S Weissman

Systematic multi-trait AAV capsid engineering for efficient gene delivery

系统性多性状AAV衣壳工程改造以实现高效基因递送

Fatma-Elzahraa Eid ,Albert T Chen ,Ken Y Chan ,Qin Huang ,Qingxia Zheng ,Isabelle G Tobey ,Simon Pacouret ,Pamela P Brauer ,Casey Keyes ,Megan Powell ,Jencilin Johnston ,Binhui Zhao ,Kasper Lage ,Alice F Tarantal ,Yujia A Chan ,Benjamin E Deverman

Spatial atlas of the mouse central nervous system at molecular resolution

分子分辨率的小鼠中枢神经系统空间图谱

Hailing Shi #, Yichun He #, Yiming Zhou #, Jiahao Huang, Kamal Maher, Brandon Wang, Zefang Tang, Shuchen Luo, Peng Tan, Morgan Wu, Zuwan Lin, Jingyi Ren, Yaman Thapa, Xin Tang, Ken Y Chan, Benjamin E Deverman, Hao Shen, Albert Liu, Jia Liu, Xiao Wang

Targeting AAV vectors to the central nervous system by engineering capsid-receptor interactions that enable crossing of the blood-brain barrier

通过设计能够穿过血脑屏障的衣壳受体相互作用,将 AAV 载体靶向中枢神经系统

Qin Huang, Albert T Chen, Ken Y Chan, Hikari Sorensen, Andrew J Barry, Bahar Azari, Qingxia Zheng, Thomas Beddow, Binhui Zhao, Isabelle G Tobey, Cynthia Moncada-Reid, Fatma-Elzahraa Eid, Christopher J Walkey, M Cecilia Ljungberg, William R Lagor, Jason D Heaney, Yujia A Chan, Benjamin E Deverman