Kidney Outcomes in Patients With Hereditary Transthyretin Amyloid Nephropathy Treated With Transthyretin Stabilizers And Gene-Silencer Therapies
采用转甲状腺素稳定剂和基因沉默疗法治疗遗传性转甲状腺素淀粉样变性肾病患者的肾脏结局
期刊:Kidney International Reports
影响因子:5.7
doi:10.1016/j.ekir.2025.03.029
Dang, Julien; Solignac, Justine; Ferlicot, Sophie; Mussini, Charlotte; Bridoux, Frank; Huart, Antoine; Essig, Marie; Campigli, Delphine; Bobot, Mickaël; Daniel, Laurent; Damy, Thibaud; Planté-Bordeneuve, Violaine; Sakhi, Hamza; Labeyrie, Céline; Cauquil, Cécile; Echaniz-Laguna, Andoni; Kounis, Ilias; Moktefi, Anissa; Devic, Perrine; Mouawad, Sarah; Brodin-Sartorius, Albane; Snanoudj, Renaud; Zaidan, Mohamad; Jourde-Chiche, Noémie; Audard, Vincent