Evaluation of AAV Capsids and Delivery Approaches for Hereditary Hemorrhagic Telangiectasia Gene Therapy.
遗传性出血性毛细血管扩张症基因治疗中AAV衣壳和递送方法的评估
期刊:Translational Stroke Research
影响因子:4.3
doi:10.1007/s12975-024-01275-4
Yadav Alka, Liang Rich, Press Kelly, Schmidt Annika, Shabani Zahra, Leng Kun, Wang Calvin, Sekhar Abinav, Shi Joshua, Devlin Garth W, Gonzalez Trevor J, Asokan Aravind, Su Hua