Zoledronate in the prevention of Paget's (ZiPP): protocol for a randomised trial of genetic testing and targeted zoledronic acid therapy to prevent SQSTM1-mediated Paget's disease of bone
唑来膦酸预防佩吉特病(ZiPP):一项随机试验方案,旨在通过基因检测和靶向唑来膦酸治疗预防SQSTM1介导的佩吉特骨病。
期刊:BMJ Open
影响因子:2.3
doi:10.1136/bmjopen-2019-030689
Cronin, Owen; Forsyth, Laura; Goodman, Kirsteen; Lewis, Steff C; Keerie, Catriona; Walker, Allan; Porteous, Mary; Cetnarskyj, Roseanne; Ranganath, Lakshminarayan R; Selby, Peter L; Hampson, Geeta; Chandra, Rama; Ho, Shu; Tobias, Jon H; Young-Min, Steven; McKenna, Malachi J; Crowley, Rachel K; Fraser, William D; Gennari, Luigi; Nuti, Ranuccio; Brandi, Maria Luisa; Del Pino-Montes, Javier; Devogelaer, Jean-Pierre; Durnez, Anne; Isaia, Giancarlo; Di Stefano, Marco; Guañabens, Núria; Blanch, Josep; Seibel, Markus J; Walsh, John P; Kotowicz, Mark A; Nicholson, Geoffrey C; Duncan, Emma L; Major, Gabor; Horne, Anne; Gilchrist, Nigel L; Boers, Maarten; Murray, Gordon D; Charnock, Keith; Wilkinson, Diana; Russell, R Graham G; Ralston, Stuart H