Vosoritide Therapy in Children with Achondroplasia: Early Experience and Practical Considerations for Clinical Practice
沃索利肽治疗儿童软骨发育不全:早期经验和临床实践中的实用考量
期刊:Advances in Therapy
影响因子:4
doi:10.1007/s12325-023-02705-9
Semler, Oliver; Cormier-Daire, Valérie; Lausch, Ekkehart; Bober, Michael B; Carroll, Ricki; Sousa, Sérgio B; Deyle, David; Faden, Maha; Hartmann, Gabriele; Huser, Aaron J; Legare, Janet M; Mohnike, Klaus; Rohrer, Tilman R; Rutsch, Frank; Smith, Pamela; Travessa, Andre M; Verardo, Angela; White, Klane K; Wilcox, William R; Hoover-Fong, Julie