ASOs are an effective treatment for disease-associated oligodendrocyte signatures in premanifest and symptomatic SCA3 mice.
ASO 可有效治疗 SCA3 前驱期和症状期小鼠的疾病相关少突胶质细胞特征
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.02.033
Schuster Kristen H, Zalon Annie J, DiFranco Danielle M, Putka Alexandra F, Stec Nicholas R, Jarrah Sabrina I, Naeem Arsal, Haque Zaid, Zhang Hanrui, Guan Yuanfang, McLoughlin Hayley S
