日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Pharmacokinetics and Safety of Selumetinib Granule Formulation in Children With Symptomatic, Inoperable Neurofibromatosis Type 1-Related Plexiform Neurofibromas (SPRINKLE; phase I/II)

Selumetinib颗粒剂治疗有症状、无法手术的1型神经纤维瘤病相关丛状神经纤维瘤患儿的药代动力学和安全性研究(SPRINKLE;I/II期)

Hernáiz Driever, Pablo; Kordes, Uwe R; Brecht, Ines B; Saletti, Veronica; Fisher, Michael J; Doughton, Gail; Arefayene, Million; Rigazio, Anna; Lluch, Nuria; Llorente, Nereida; Diede, Scott J; Salvador, Hector

Spatial Relations between Coccoliths and Their Confining Membrane During Crystal Morphogenesis

球石藻与其包被膜在晶体形态发生过程中的空间关系

Avrahami, Emanuel M; Karpov, Dmitry; Aram, Lior; Elad, Nadav; Safadi, Razi; Rosenhek-Goldian, Irit; Sui, Xiao-Meng; de Haan, Diede; Varsano, Neta; Cohen, Sidney R; Zlotnikov, Igor; Gal, Assaf

Templateless crystallization of holococcolith crystals visualized by intracellular site-specific three-dimensional microscopy

利用细胞内位点特异性三维显微镜观察全球石晶体的无模板结晶过程

Ben-Joseph, Oz; Meng, Yu-Feng; Aram, Lior; Abu Freha, Ikhlas; Lansky, Zipora; Safadi, Razi; de Haan, Diede; Rechav, Katya; Kaplan-Ashiri, Ifat; Varsano, Neta; Gal, Assaf

Generation of In Vivo-Inspired 3D Collagen Models for Guided Tumor Invasion In Vitro

构建体内启发式3D胶原蛋白模型用于体外引导肿瘤侵袭

den Daas, Stijn; Bakker, Gert-Jan; van Ens, Diede; Grosu, Eleni-Andria; Vullings, Manon; Beunk, Lianne; Friedl, Peter; Wolf, Katarina

Efficacy and safety of selumetinib in adults with neurofibromatosis type 1 and symptomatic, inoperable plexiform neurofibromas (KOMET): a multicentre, international, randomised, placebo-controlled, parallel, double-blind, phase 3 study

selumetinib治疗1型神经纤维瘤病合并症状性、不可手术切除的丛状神经纤维瘤成人患者的疗效和安全性(KOMET):一项多中心、国际性、随机、安慰剂对照、平行、双盲3期研究

Chen, Alice P; Coyne, Geraldine O'Sullivan; Wolters, Pamela L; Martin, Staci; Farschtschi, Said; Blanco, Ignacio; Chen, Zhongping; Darrigo, Luiz Guilherme Jr; Eoli, Marica; Whittle, James R; Nishida, Yoshihiro; Lamarca, Rosa; de la Rosa Rodriguez, Randolph; Adeyemi, Ayo; Herrero, Idoia; Llorente, Nereida; Diede, Scott J; Dombi, Eva; Wolkenstein, Pierre

C9orf72 hexanucleotide repeat expansions impair microglial response in ALS.

C9orf72 六核苷酸重复序列扩增会损害 ALS 中的小胶质细胞反应。

Masrori Pegah, Bijnens Baukje, Fumagalli Laura, Davie Kristofer, Poovathingal Suresh Kumar, Meese Tim, Storm Annet, Hersmus Nicole, Fazal Raheem, van den Biggelaar Diede, Asselbergh Bob, Gruel Roxane, Van Den Daele Johanna, Denton Heidi, Miquel Paula Polanco, Manzella Simona, De Vos Winnok H, Chandran Siddhartan, Van Den Bosch Ludo, Thal Dietmar Rudolf, Mancuso Renzo, Van Damme Philip

Cell-specific Eif2b5 mutant mice: novel insights into roles of macroglia in vanishing white matter

细胞特异性 Eif2b5 突变小鼠:对巨噬细胞在白质消失中的作用的新见解

Triñanes-Ramos, Javier; Bugiani, Marianna; van Rooijen-van Leeuwen, Gemma M; Chevalier, Juliette A; Siu, Yuan Jiew; van Utenhove, Elise L H; Hoogterp, Leoni; Witkamp, Diede; Oudejans, Ellen; Lodder, Bastiaan; Kole, Maarten H P; Saher, Gesine; Nave, Klaus-Armin; Abbink, Truus E M; van der Knaap, Marjo S

Neocortical tau propagation is a mediator of clinical heterogeneity in Alzheimer's disease

新皮质tau蛋白扩散是阿尔茨海默病临床异质性的介质

Anjalika Chongtham ,Aarthi Ramakrishnan ,Marissa Farinas ,Diede W M Broekaart ,Joon Ho Seo ,Carolyn W Zhu ,Mary Sano ,Li Shen ,Ana C Pereira

Molecular signatures of regional vulnerability to tauopathy in excitatory cortical neurons.

兴奋性皮层神经元中tau蛋白病变区域易感性的分子特征。

Broekaart Diede W M, Sharma Abhijeet, Ramakrishnan Aarthi, Chongtham Anjalika, Günther Dorothee M, Subramaniyan Saraswathi, Wang Minghui, Patel Vishwendra, Zhang Bin, Grinberg Lea T, Blitzer Robert D, Schmidt Eric F, Shen Li, Hof Patrick R, Pereira Ana C

Good manufacturing practice production of an off-the-shelf CD34(+) progenitor-derived NK cell product with preserved anti-tumor functionality post-infusion in NOD/SCID/IL2Rg(null) mice.

按照良好生产规范生产现成的 CD34(+) 祖细胞衍生 NK 细胞产品,该产品在输注到 NOD/SCID/IL2Rg(null) 小鼠后仍保持抗肿瘤功能

Hooijmaijers Laura, Vidal-Manrique Marcos, Spils Bart, van Ens Diede, Rodriguez Verónica Castaño, Hobo Willemijn, de Goede Anna L, van Dorp Suzanne, Jansen Joop H, van der Waart Anniek B, de Jonge Paul K J D, Dolstra Harry