Allele-Selective Suppression of Mutant Huntingtin in Primary Human Blood Cells
等位基因选择性抑制原代人血细胞中的突变亨廷顿蛋白
期刊:Scientific Reports
影响因子:3.9
doi:10.1038/srep46740
Miller, James R C; Pfister, Edith L; Liu, Wanzhao; Andre, Ralph; Träger, Ulrike; Kennington, Lori A; Lo, Kimberly; Dijkstra, Sipke; Macdonald, Douglas; Ostroff, Gary; Aronin, Neil; Tabrizi, Sarah J