Allosteric folding correction of F508del and rare CFTR mutants by elexacaftor-tezacaftor-ivacaftor (Trikafta) combination
通过 elexacaftor-tezacaftor-ivacaftor (Trikafta) 组合对 F508del 和罕见 CFTR 突变体进行变构折叠校正
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.139983
Guido Veit, Ariel Roldan, Mark A Hancock, Dillon F Da Fonte, Haijin Xu, Maytham Hussein, Saul Frenkiel, Elias Matouk, Tony Velkov, Gergely L Lukacs