Di-valent siRNA-mediated silencing of MSH3 blocks somatic repeat expansion in mouse models of Huntington's disease
二价 siRNA 介导的 MSH3 沉默可阻断亨廷顿氏病小鼠模型中的体细胞重复扩增
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2023.05.006
Daniel O'Reilly, Jillian Belgrad, Chantal Ferguson, Ashley Summers, Ellen Sapp, Cassandra McHugh, Ella Mathews, Adel Boudi, Julianna Buchwald, Socheata Ly, Dimas Moreno, Raymond Furgal, Eric Luu, Zachary Kennedy, Vignesh Hariharan, Kathryn Monopoli, X William Yang, Jeffery Carroll, Marian DiFiglia,
