Vitreal delivery of AAV vectored Cnga3 restores cone function in CNGA3-/-/Nrl-/- mice, an all-cone model of CNGA3 achromatopsia
玻璃体内注射AAV载体Cnga3可恢复CNGA3-/-/Nrl-/-小鼠(一种CNGA3全视锥细胞模型)的视锥细胞功能。
期刊:Human Molecular Genetics
影响因子:3.2
doi:10.1093/hmg/ddv114
Du, Wei; Tao, Ye; Deng, Wen-Tao; Zhu, Ping; Li, Jie; Dai, Xufeng; Zhang, Yuxin; Shi, Wei; Liu, Xuan; Chiodo, Vince A; Ding, Xi-Qin; Zhao, Chen; Michalakis, Stylianos; Biel, Martin; Zhang, Zuoming; Qu, Jia; Hauswirth, William W; Pang, Ji-Jing