mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency
mRNA 疗法改善 Citrin 缺乏症小鼠模型中的代谢和行为异常
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2019.04.017
Jingsong Cao, Ding An, Mikel Galduroz, Jenny Zhuo, Shi Liang, Marianne Eybye, Andrea Frassetto, Eishi Kuroda, Aki Funahashi, Jordan Santana, Cosmin Mihai, Kerry E Benenato, E Sathyajith Kumarasinghe, Staci Sabnis, Timothy Salerno, Kimberly Coughlan, Edward J Miracco, Becca Levy, Gilles Besin, Joshua