Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy
体细胞基因编辑可改善猪和人类杜氏肌营养不良症模型中的骨骼和心肌衰竭
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-019-0738-2
A Moretti #, L Fonteyne #, F Giesert #, P Hoppmann #, A B Meier #, T Bozoglu, A Baehr, C M Schneider, D Sinnecker, K Klett, T Fröhlich, F Abdel Rahman, T Haufe, S Sun, V Jurisch, B Kessler, R Hinkel, R Dirschinger, E Martens, C Jilek, A Graf, S Krebs, G Santamaria, M Kurome, V Zakhartchenko, B Campb