Enzyme Replacement Therapy in a Patient with Gaucher Disease Type III: A Paradigmatic Case Showing Severe Adverse Reactions Started a Long Time After the Beginning of Treatment
戈谢病III型患者的酶替代疗法:一个典型病例,显示严重不良反应在治疗开始很久之后才出现
期刊:JIMD Reports
影响因子:1.8
doi:10.1007/8904_2013_214
Vairo, Filippo; Netto, Cristina; Dorneles, Alicia; Mittelstadt, Suzana; Wilke, Matheus; Doneda, Divair; Michelin, Kristiane; Ribeiro, Camila Blos; Quevedo, Amanda; Vieira, Tatiane; Nalin, Tatiele; Lueska, Sônia; Schwartz, Ida Vanessa D