日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Combined Loss of Obsc and Obsl1 in Murine Hearts Results in Diastolic Dysfunction, Altered Metabolism, and Deregulated Mitophagy

小鼠心脏中 Obsc 和 Obsl1 的联合缺失会导致舒张功能障碍、代谢改变和线粒体自噬失调

Fujita, Kyohei; Desmond, Patrick; Blondelle, Jordan; Soták, Matúš; Rajan, Meenu Rohini; Clark, Madison; Estève, Éric; Chan, Yunghang; Gu, Yusu; Actis Dato, Virginia; Marrocco, Valeria; Dalton, Nancy D; Ghassemian, Majid; Do, Aryanne; Klos, Matthew; Peterson, Kirk L; Sheikh, Farah; Cho, Yoshitake; Börgeson, Emma; Lange, Stephan

Preclinical efficacy and safety of AAVrh10-based plakophilin-2 gene therapy (LX2020) as a treatment for arrhythmogenic cardiomyopathy.

基于 AAVrh10 的 plakophilin-2 基因疗法 (LX2020) 治疗致心律失常性心肌病的临床前疗效和安全性

Zhang Jing, Gutierrez-Lara Erika Joana, Do Aryanne, Nguyen Lena, Nair Anju, Selvan Nithya, Fenn Tim, Adler Eric, Khanna Richie, Sheikh Farah