日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Protein Assembly Modulation: A New Approach to Amyotrophic Lateral Sclerosis (ALS) Therapeutics

蛋白质组装调控:肌萎缩侧索硬化症(ALS)治疗的新方法

Yu, Shao Feng; Paulvannan, Kumar; Solas, Dennis; Lingappa, Anuradha F; Moreira, Ana Raquel; Sahu, Shriya; Michon, Maya; Macieik, Amanda; Goldsmith, Danielle; DeYarman, Nicholas; Mallesh, Suguna; Prasad, M Dharma; Maios, Claudia; Ruan, Kai; Tomassy, Giulio S; Jensen, Elizabeth; McGuirk, Emma; Bader, Verian; Mueller-Schiffmann, Andreas; Reed, Jonathan C; Lingappa, Jaisri R; Asundi, Vinod; Hong, Shi; Jacobsen, Steve; Brandon, Nicholas; Ostrow, Lyle; Lloyd, Tom; Parker, J Alex; Staats, Kim A; Ichida, Justin; Dodge, James C; Dey, Debendranath; Korth, Carsten; Selvarajah, Suganya; Lingappa, Vishwanath R; Rosenfeld, Jeffrey

Lipid Involvement in Neurodegenerative Diseases of the Motor System: Insights from Lysosomal Storage Diseases

脂质在运动系统神经退行性疾病中的作用:来自溶酶体贮积症的启示

Dodge, James C

Systemic administration of a recombinant AAV1 vector encoding IGF-1 improves disease manifestations in SMA mice

系统性注射编码IGF-1的重组AAV1载体可改善SMA小鼠的疾病症状。

Tsai, Li-Kai; Chen, Chien-Lin; Ting, Chen-Hung; Lin-Chao, Sue; Hwu, Wuh-Liang; Dodge, James C; Passini, Marco A; Cheng, Seng H

Gene transfer to the CNS is efficacious in immune-primed mice harboring physiologically relevant titers of anti-AAV antibodies

在体内含有生理相关滴度抗AAV抗体的免疫预激活小鼠中,基因转移到中枢神经系统是有效的。

Treleaven, Christopher M; Tamsett, Thomas J; Bu, Jie; Fidler, Jonathan A; Sardi, S Pablo; Hurlbut, Gregory D; Woodworth, Lisa A; Cheng, Seng H; Passini, Marco A; Shihabuddin, Lamya S; Dodge, James C

Disease progression in a mouse model of amyotrophic lateral sclerosis: the influence of chronic stress and corticosterone.

肌萎缩侧索硬化症小鼠模型中的疾病进展:慢性应激和皮质酮的影响

Fidler Jonathan A, Treleaven Christopher M, Frakes Ashley, Tamsett Thomas J, McCrate Mary, Cheng Seng H, Shihabuddin Lamya S, Kaspar Brian K, Dodge James C

Comparative analysis of acid sphingomyelinase distribution in the CNS of rats and mice following intracerebroventricular delivery

脑室内给药后大鼠和小鼠中枢神经系统酸性鞘磷脂酶分布的比较分析

Treleaven, Christopher M; Tamsett, Thomas; Fidler, Jonathan A; Taksir, Tatyana V; Cheng, Seng H; Shihabuddin, Lamya S; Dodge, James C

Delivery of AAV-IGF-1 to the CNS extends survival in ALS mice through modification of aberrant glial cell activity

将AAV-IGF-1递送至中枢神经系统可通过调节异常的神经胶质细胞活性延长ALS小鼠的生存期。

Dodge, James C; Haidet, Amanda M; Yang, Wendy; Passini, Marco A; Hester, Mark; Clarke, Jennifer; Roskelley, Eric M; Treleaven, Christopher M; Rizo, Liza; Martin, Heather; Kim, Soo H; Kaspar, Rita; Taksir, Tatyana V; Griffiths, Denise A; Cheng, Seng H; Shihabuddin, Lamya S; Kaspar, Brian K

Temporal neuropathologic and behavioral phenotype of 6neo/6neo Pompe disease mice

6neo/6neo庞贝病小鼠的时间神经病理学和行为表型

Sidman, Richard L; Taksir, Tatyana; Fidler, Jonathan; Zhao, Michael; Dodge, James C; Passini, Marco A; Raben, Nina; Thurberg, Beth L; Cheng, Seng H; Shihabuddin, Lamya S

Gene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease

人类酸性鞘磷脂酶基因转移可纠正尼曼-匹克A型疾病小鼠模型中的神经病理学和运动障碍。

Dodge, James C; Clarke, Jennifer; Song, Antonius; Bu, Jie; Yang, Wendy; Taksir, Tatyana V; Griffiths, Denise; Zhao, Michael A; Schuchman, Edward H; Cheng, Seng H; O'Riordan, Catherine R; Shihabuddin, Lamya S; Passini, Marco A; Stewart, Gregory R