Cyclic mismatch binding ligands interact with disease-associated CGG trinucleotide repeats in RNA and suppress their translation
环状错配结合配体与 RNA 中与疾病相关的 CGG 三核苷酸重复序列相互作用并抑制其翻译
期刊:Nucleic Acids Research
影响因子:16.6
doi:10.1093/nar/gkab669
Patryk Konieczny, Sanjukta Mukherjee, Ewa Stepniak-Konieczna, Katarzyna Taylor, Daria Niewiadomska, Agnieszka Piasecka, Agnieszka Walczak, Anna Baud, Chikara Dohno, Kazuhiko Nakatani, Krzysztof Sobczak