日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A magnetic separation method for isolating and characterizing the biomolecular corona of lipid nanoparticles

一种分离和表征脂质纳米粒子生物分子冠的磁分离方法

Valentina Francia #, Yao Zhang #, Miffy Hok Yan Cheng, Raymond M Schiffelers, Dominik Witzigmann, Pieter R Cullis

Lipid Nanoparticle-Mediated Hit-and-Run Approaches Yield Efficient and Safe In Situ Gene Editing in Human Skin

脂质纳米粒子介导的“打了就跑”方法可在人体皮肤中实现高效、安全的原位基因编辑

Juliana Bolsoni, Danny Liu, Fatemeh Mohabatpour, Ronja Ebner, Gaurav Sadhnani, Belal Tafech, Jerry Leung, Selina Shanta, Kevin An, Tessa Morin, Yihang Chen, Alfonso Arguello, Keith Choate, Eric Jan, Colin J D Ross, Davide Brambilla, Dominik Witzigmann, Jayesh Kulkarni, Pieter R Cullis, Sarah Hedtric

Lipid nanoparticle-mediated silencing of osteogenic suppressor GNAS leads to osteogenic differentiation of mesenchymal stem cells in vivo

脂质纳米粒子介导的成骨抑制因子 GNAS 的沉默导致体内间充质干细胞的成骨分化

Genc Basha, Andrew G Cottle, Thavaneetharajah Pretheeban, Karen Yt Chan, Dominik Witzigmann, Robert N Young, Fabio Mv Rossi, Pieter R Cullis

Spray drying siRNA-lipid nanoparticles for dry powder pulmonary delivery

喷雾干燥 siRNA-脂质纳米颗粒用于干粉肺部输送

Christoph M Zimmermann, Domizia Baldassi, Karen Chan, Nathan B P Adams, Alina Neumann, Diana Leidy Porras-Gonzalez, Xin Wei, Nikolaus Kneidinger, Mircea Gabriel Stoleriu, Gerald Burgstaller, Dominik Witzigmann, Paola Luciani, Olivia M Merkel

In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levels

恒河猴体内 PCSK9 腺嘌呤碱基编辑可降低 LDL 胆固醇水平

Tanja Rothgangl, Melissa K Dennis, Paulo J C Lin, Rurika Oka, Dominik Witzigmann, Lukas Villiger, Weihong Qi, Martina Hruzova, Lucas Kissling, Daniela Lenggenhager, Costanza Borrelli, Sabina Egli, Nina Frey, Noëlle Bakker, John A Walker 2nd, Anastasia P Kadina, Denis V Victorov, Martin Pacesa, Susan

In vivo cytidine base editing of hepatocytes without detectable off-target mutations in RNA and DNA

肝细胞体内胞苷碱基编辑,RNA 和 DNA 中未检测到脱靶突变

Lukas Villiger #, Tanja Rothgangl #, Dominik Witzigmann, Rurika Oka, Paulo J C Lin, Weihong Qi, Sharan Janjuha, Christian Berk, Femke Ringnalda, Mitchell B Beattie, Markus Stoffel, Beat Thöny, Jonathan Hall, Hubert Rehrauer, Ruben van Boxtel, Ying K Tam, Gerald Schwank3

Non-viral gene delivery of the oncotoxic protein NS1 for treatment of hepatocellular carcinoma

非病毒基因传递癌毒性蛋白 NS1 用于治疗肝细胞癌

Dominik Witzigmann, Philip Grossen, Cristina Quintavalle, Manuela Lanzafame, Susanne H Schenk, Xue-Ting Tran, Bernhard Englinger, Patrick Hauswirth, David Grünig, Sushilla van Schoonhoven, Stephan Krähenbühl, Luigi M Terracciano, Walter Berger, Salvatore Piscuoglio, Luca Quagliata, Jean Rommelaere, 

FAM13A as potential therapeutic target in modulating TGF-β-induced airway tissue remodeling in COPD

FAM13A 作为调节 TGF-β 诱导的 COPD 气道组织重塑的潜在治疗靶点

Anthony Tam, Pascal Leclair, Ling Vicky Li, Chen X Yang, Xuan Li, Dominik Witzigmann, Jayesh A Kulkarni, Tillie-Louise Hackett, Delbert R Dorscheid, Gurpreet K Singhera, James C Hogg, Pieter R Cullis, Don D Sin, Chinten James Lim