日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A novel rhesus macaque model of Huntington's disease recapitulates key neuropathological changes along with motor and cognitive decline.

一种新型的恒河猴亨廷顿病模型重现了关键的神经病理学变化以及运动和认知能力的下降

Weiss Alison R, Liguore William A, Brandon Kristin, Wang Xiaojie, Liu Zheng, Domire Jacqueline S, Button Dana, Srinivasan Sathya, Kroenke Christopher D, McBride Jodi L

Implications of microscale lung damage for COVID-19 pulmonary ventilation dynamics: A narrative review

微尺度肺损伤对 COVID-19 肺通气动力学的影响:叙述性综述

Dimbath, Elizabeth; Maddipati, Veeranna; Stahl, Jennifer; Sewell, Kerry; Domire, Zachary; George, Stephanie; Vahdati, Ali

Intra-striatal AAV2.retro administration leads to extensive retrograde transport in the rhesus macaque brain: implications for disease modeling and therapeutic development.

纹状体内 AAV2.retro 给药可导致恒河猴脑内广泛的逆行运输:对疾病建模和治疗开发的意义

Weiss Alison R, Liguore William A, Domire Jacqueline S, Button Dana, McBride Jodi L

AAV-PHP.B Administration Results in a Differential Pattern of CNS Biodistribution in Non-human Primates Compared with Mice

与小鼠相比,AAV-PHP.B 给药导致非人灵长类动物中枢神经系统生物分布模式的差异

Liguore, William A; Domire, Jacqueline S; Button, Dana; Wang, Yun; Dufour, Brett D; Srinivasan, Sathya; McBride, Jodi L

AAV-mediated follistatin gene therapy improves functional outcomes in the TIC-DUX4 mouse model of FSHD

AAV 介导的卵泡抑素基因治疗可改善 TIC-DUX4 小鼠 FSHD 模型的功能结果

Carlee R Giesige, Lindsay M Wallace, Kristin N Heller, Jocelyn O Eidahl, Nizar Y Saad, Allison M Fowler, Nettie K Pyne, Mustafa Al-Kharsan, Afrooz Rashnonejad, Gholamhossein Amini Chermahini, Jacqueline S Domire, Diana Mukweyi, Sara E Garwick-Coppens, Susan M Guckes, K John McLaughlin, Kathrin Meyer

Discovery of a CLN7 model of Batten disease in non-human primates.

在非人灵长类动物中发现了 CLN7 型巴顿病模型

McBride Jodi L, Neuringer Martha, Ferguson Betsy, Kohama Steven G, Tagge Ian J, Zweig Robert C, Renner Laurie M, McGill Trevor J, Stoddard Jonathan, Peterson Samuel, Su Weiping, Sherman Larry S, Domire Jacqueline S, Ducore Rebecca M, Colgin Lois M, Lewis Anne D

Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD

临床前安全性和脱靶研究,以支持 AAV 介导的 RNAi 疗法在 FSHD 中的应用

Lindsay M Wallace, Nizar Y Saad, Nettie K Pyne, Allison M Fowler, Jocelyn O Eidahl, Jacqueline S Domire, Danielle A Griffin, Adam C Herman, Zarife Sahenk, Louise R Rodino-Klapac, Scott Q Harper

Human genome meeting 2016 : Houston, TX, USA. 28 February - 2 March 2016

2016年人类基因组会议:美国德克萨斯州休斯顿,2016年2月28日至3月2日

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Zhu, Y; Zhao, J; Calhoun, V; Xiong, M; Dobretsberger, O; Egger, M; Leimgruber, F; Sadedin, S; Oshlack, A; Antonio, V A A; Ono, N; Ahmed, Z; Bolisetty, M; Zeeshan, S; Anguiano, E; Ucar, D; Sarkar, A; Nandineni, M R; Zeng, C; Shao, J; Cao, H; Hastie, A; Pang, A W; Lam, E T; Liang, T; Pham, K; Saghbini, M; Dzakula, Z; Chee-Wei, Y; Dongsheng, L; Lai-Ping, W; Lian, D; Hee, R O Twee; Yunus, Y; Aghakhanian, F; Mokhtar, S S; Lok-Yung, C V; Bhak, J; Phipps, M; Shuhua, X; Yik-Ying, T; Kumar, V; Boon-Peng, H; Campbell, I; Young, M -A; James, P; Rain, M; Mohammad, G; Kukreti, R; Pasha, Q; Akilzhanova, A R; Guelly, C; Abilova, Z; Rakhimova, S; Akhmetova, A; Kairov, U; Trajanoski, S; Zhumadilov, Z; Bekbossynova, M; Schumacher, C; Sandhu, S; Harkins, T; Makarov, V; Doddapaneni, H; Glenn, R; Momin, Z; Dilrukshi, B; Chao, H; Meng, Q; Gudenkauf, B; Kshitij, R; Jayaseelan, J; Nessner, C; Lee, S; Blankenberg, K; Lewis, L; Hu, J; Han, Y; Dinh, H; Jireh, S; Walker, K; Boerwinkle, E; Muzny, D; Gibbs, R; Hu, J; 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Mouse Dux is myotoxic and shares partial functional homology with its human paralog DUX4

小鼠 Dux 具有肌毒性,与人类旁系同源物 DUX4 具有部分功能同源性

Jocelyn O Eidahl, Carlee R Giesige, Jacqueline S Domire, Lindsay M Wallace, Allison M Fowler, Susan M Guckes, Sara E Garwick-Coppens, Paul Labhart, Scott Q Harper

Effect of collagen digestion on the passive elastic properties of diaphragm muscle in rat

胶原蛋白消化对大鼠膈肌被动弹性特性的影响

Rowe, Justin; Chen, Qingshan; Domire, Zachary J; McCullough, Matthew B; Sieck, Gary; Zhan, Wen-Zhi; An, Kai-Nan