Stable human FIX expression after 0.9G intrauterine gene transfer of self-complementary adeno-associated viral vector 5 and 8 in macaques
0.9G 自互补腺相关病毒载体 5 和 8 在恒河猴宫内进行基因转移后稳定表达人 FIX
期刊:Molecular Therapy
影响因子:12.1
doi:10.1038/mt.2011.107
Citra N Z Mattar, Amit C Nathwani, Simon N Waddington, Niraja Dighe, Christine Kaeppel, Ali Nowrouzi, Jenny Mcintosh, Nuryanti B Johana, Bryan Ogden, Nicholas M Fisk, Andrew M Davidoff, Anna David, Donald Peebles, Marcus B Valentine, Jens-Uwe Appelt, Christof von Kalle, Manfred Schmidt, Arijit Biswa