Maralixibat for the treatment of PFIC: Long-term, IBAT inhibition in an open-label, Phase 2 study
Maralixibat 用于治疗 PFIC:一项开放标签的 II 期研究的长期 IBAT 抑制研究
期刊:Hepatology Communications
影响因子:4.6
doi:10.1002/hep4.1980
Loomes, Kathleen M; Squires, Robert H; Kelly, Deirdre; Rajwal, Sanjay; Soufi, Nisreen; Lachaux, Alain; Jankowska, Irena; Mack, Cara; Setchell, Kenneth D R; Karthikeyan, Palaniswamy; Kennedy, Ciara; Dorenbaum, Alejandro; Desai, Nirav K; Garner, Will; Jaecklin, Thomas; Vig, Pamela; Miethke, Alexander; Thompson, Richard J