日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cytosine base editing inhibits hepatitis B virus replication and reduces HBsAg expression in vitro and in vivo

胞嘧啶碱基编辑抑制乙肝病毒复制并降低体内外 HBsAg 表达

Elena M Smekalova, Maria G Martinez, Emmanuel Combe, Anuj Kumar, Selam Dejene, Dominique Leboeuf, Chao-Ying Chen, J Robert Dorkin, Lan Shuan Shuang, Sarah Kieft, Lauren Young, Luis Alberto Barrera, Michael S Packer, Giuseppe Ciaramella, Barbara Testoni, Francine Gregoire, Fabien Zoulim

A BURST-BAUS consensus document for best practice in the conduct of scrotal exploration for suspected testicular torsion: the Finding consensus for orchIdopeXy In Torsion (FIX-IT) study

BURST-BAUS共识文件:疑似睾丸扭转阴囊探查术最佳实践指南:睾丸扭转固定术(FIX-IT)研究共识

Clement, Keiran D; Light, Alexander; Asif, Aqua; Chan, Vinson Wai-Shun; Khadhouri, Sinan; Shah, Taimur T; Banks, Frederick; Dorkin, Trevor; Driver, Christopher P; During, Vinnie; Fraser, Nia; Johnston, Maximilian J; Lucky, Marc; Modgil, Vaibhav; Muneer, Asif; Parnham, Arie; Pearce, Ian; Shabbir, Majed; Shenoy, Manoj; Summerton, Duncan J; Undre, Shabnam; Williams, Alun; MacLennan, Steven; Kasivisvanathan, Veeru

Occupational Hearing Loss for Platinum Miners in South Africa: A Case Study of Data Sharing Practices and Ethical Challenges in the Mining Industry

南非铂金矿工人的职业性听力损失:采矿业数据共享实践和伦理挑战案例研究

Ntlhakana, Liepollo; Nelson, Gill; Khoza-Shangase, Katijah; Dorkin, Elton

Functionalized lipid-like nanoparticles for in vivo mRNA delivery and base editing

用于体内 mRNA 递送和碱基编辑的功能化类脂质纳米粒子

Xinfu Zhang, Weiyu Zhao, Giang N Nguyen, Chengxiang Zhang, Chunxi Zeng, Jingyue Yan, Shi Du, Xucheng Hou, Wenqing Li, Justin Jiang, Binbin Deng, David W McComb, Robert Dorkin, Aalok Shah, Luis Barrera, Francine Gregoire, Manmohan Singh, Delai Chen, Denise E Sabatino, Yizhou Dong5

Lung transplant referral practice patterns: a survey of cystic fibrosis physicians and general pulmonologists

肺移植转诊实践模式:囊性纤维化医生和普通肺科医生的调查

Bartley, Bethany L; Schwartz, Carolyn E; Stark, Roland B; Georgiopoulos, Anna M; Friedman, Deborah; Richards, Christopher J; Dorkin, Henry L; Kinane, T Bernard; Neuringer, Isabel P; Yonker, Lael M

Rapid, Single-Cell Analysis and Discovery of Vectored mRNA Transfection In Vivo with a loxP-Flanked tdTomato Reporter Mouse

利用loxP侧翼tdTomato报告基因小鼠进行体内载体化mRNA转染的快速单细胞分析和发现

Kauffman, Kevin J; Oberli, Matthias A; Dorkin, J Robert; Hurtado, Juan E; Kaczmarek, James C; Bhadani, Shivani; Wyckoff, Jeff; Langer, Robert; Jaklenec, Ana; Anderson, Daniel G

Lipid Nanoparticle Assisted mRNA Delivery for Potent Cancer Immunotherapy

脂质纳米颗粒辅助 mRNA 递送,实现强效癌症免疫疗法

Matthias A Oberli, Andreas M Reichmuth, J Robert Dorkin, Michael J Mitchell, Owen S Fenton, Ana Jaklenec, Daniel G Anderson, Robert Langer, Daniel Blankschtein

Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo

通过病毒和非病毒联合递送 CRISPR 系统成分在体内进行治疗性基因组编辑

Hao Yin, Chun-Qing Song, Joseph R Dorkin, Lihua J Zhu, Yingxiang Li, Qiongqiong Wu, Angela Park, Junghoon Yang, Sneha Suresh, Aizhan Bizhanova, Ankit Gupta, Mehmet F Bolukbasi, Stephen Walsh, Roman L Bogorad, Guangping Gao, Zhiping Weng, Yizhou Dong, Victor Koteliansky, Scot A Wolfe, Robert Langer, 

Poly(glycoamidoamine) Brushes Formulated Nanomaterials for Systemic siRNA and mRNA Delivery in Vivo

聚(糖胺胺)刷配制纳米材料用于体内系统性siRNA和mRNA递送

Dong, Yizhou; Dorkin, J Robert; Wang, Weiheng; Chang, Philip H; Webber, Matthew J; Tang, Benjamin C; Yang, Junghoon; Abutbul-Ionita, Inbal; Danino, Dganit; DeRosa, Frank; Heartlein, Michael; Langer, Robert; Anderson, Daniel G

Inhaled alpha1-proteinase inhibitor therapy in patients with cystic fibrosis

吸入α1-蛋白酶抑制剂治疗囊性纤维化患者

Gaggar, Amit; Chen, Junliang; Chmiel, James F; Dorkin, Henry L; Flume, Patrick A; Griffin, Rhonda; Nichols, David; Donaldson, Scott H