日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

High-content screening identifies a small molecule that restores AP-4-dependent protein trafficking in neuronal models of AP-4-associated hereditary spastic paraplegia

高内涵筛选鉴定出一种小分子,该小分子可恢复AP-4相关遗传性痉挛性截瘫神经元模型中AP-4依赖性蛋白质运输。

Afshin Saffari ,Barbara Brechmann ,Cedric Böger ,Wardiya Afshar Saber ,Hellen Jumo ,Dosh Whye ,Delaney Wood ,Lara Wahlster ,Julian E Alecu ,Marvin Ziegler ,Marlene Scheffold ,Kellen Winden ,Jed Hubbs ,Elizabeth D Buttermore ,Lee Barrett ,Georg H H Borner ,Alexandra K Davies ,Darius Ebrahimi-Fakhari ,Mustafa Sahin

Cortical neurons obtained from patient-derived iPSCs with GNAO1 p.G203R variant show altered differentiation and functional properties

从具有 GNAO1 p.G203R 变体的患者来源的 iPSC 中获得的皮质神经元表现出改变的分化和功能特性

Maria Cristina Benedetti, Tiziano D'andrea, Alessio Colantoni, Denis Silachev, Valeria de Turris, Zaira Boussadia, Valentina A Babenko, Egor A Volovikov, Lilia Belikova, Alexandra N Bogomazova, Rita Pepponi, Dosh Whye, Elizabeth D Buttermore, Gian Gaetano Tartaglia, Maria A Lagarkova, Vladimir L Kat

High-Content Small Molecule Screen Identifies a Novel Compound That Restores AP-4-Dependent Protein Trafficking in Neuronal Models of AP-4-Associated Hereditary Spastic Paraplegia

高内涵小分子筛选鉴定出一种新型化合物,可在 AP-4 相关遗传性痉挛性截瘫的神经元模型中恢复 AP-4 依赖性蛋白质运输

Afshin Saffari, Barbara Brechmann, Cedric Boeger, Wardiya Afshar Saber, Hellen Jumo, Dosh Whye, Delaney Wood, Lara Wahlster, Julian Alecu, Marvin Ziegler, Marlene Scheffold, Kellen Winden, Jed Hubbs, Elizabeth Buttermore, Lee Barrett, Georg Borner, Alexandra Davies, Mustafa Sahin, Darius Ebrahimi-Fa

A Robust Pipeline for the Multi-Stage Accelerated Differentiation of Functional 3D Cortical Organoids from Human Pluripotent Stem Cells

人类多能干细胞多阶段加速分化功能性 3D 皮质类器官的稳健流程

Dosh Whye, Delaney Wood, Wardiya Afshar Saber, Erika M Norabuena, Nina R Makhortova, Mustafa Sahin, Elizabeth D Buttermore

Dynamic 3D Combinatorial Generation of hPSC-Derived Neuromesodermal Organoids With Diverse Regional and Cellular Identities

具有不同区域和细胞特征的 hPSC 衍生神经中胚层类器官的动态 3D 组合生成

Dosh Whye, Delaney Wood, Kristina H Kim, Cidi Chen, Nina Makhortova, Mustafa Sahin, Elizabeth D Buttermore

Applying Deep Neural Network Analysis to High-Content Image-Based Assays

将深度神经网络分析应用于高内涵图像检测

Samuel J Yang, Scott L Lipnick, Nina R Makhortova, Subhashini Venugopalan, Minjie Fan, Zan Armstrong, Thorsten M Schlaeger, Liyong Deng, Wendy K Chung, Liadan O'Callaghan, Anton Geraschenko, Dosh Whye, Marc Berndl, Jon Hazard, Brian Williams, Arunachalam Narayanaswamy, D Michael Ando, Philip Nelson,

Efficient differentiation of mouse embryonic stem cells into motor neurons

小鼠胚胎干细胞高效分化为运动神经元

Chia-Yen Wu, Dosh Whye, Robert W Mason, Wenlan Wang

Proteomic assessment of a cell model of spinal muscular atrophy

脊髓性肌萎缩症细胞模型的蛋白质组学评估

Chia-Yen Wu, Dosh Whye, Lisa Glazewski, Leila Choe, Douglas Kerr, Kelvin H Lee, Robert W Mason, Wenlan Wang