Rescue of gene-expression changes in an induced mouse model of spinal muscular atrophy by an antisense oligonucleotide that promotes inclusion of SMN2 exon 7
通过促进 SMN2 外显子 7 的纳入的反义寡核苷酸挽救脊髓性肌萎缩症诱发小鼠模型中的基因表达变化
期刊:Genomics
影响因子:3.4
doi:10.1016/j.ygeno.2015.01.007
John F Staropoli, Huo Li, Seung J Chun, Norm Allaire, Patrick Cullen, Alice Thai, Christina M Fleet, Yimin Hua, C Frank Bennett, Adrian R Krainer, Doug Kerr, Alexander McCampbell, Frank Rigo, John P Carulli
