日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Antisense oligonucleotides directed against App and Rab5 normalized endosomal Rab activity and reversed DS-AD-linked degenerative phenotypes in the Dp16 mouse model of Down syndrome.

针对 App 和 Rab5Â 的反义寡核苷酸可使内体 Rab 活性正常化,并逆转唐氏综合征 Dp16 小鼠模型中与 DS-AD 相关的退行性表型

Chen Xu-Qiao, Zuo Xinxin, Becker Ann, Mante Michael, Florio Jazmin B, Jadhav Satish G, Albay Ricardo, Johnstone Aaron, Karachentsev Dmitry, Rissman Robert, Zhao Hien, Dowdy Steven F, Mobley William C

Stereopure ASOs: An unanticipated increase in selectivity for targeting mutant HTT

立体纯反义寡核苷酸:靶向突变型HTT选择性意外提高

Gulumkar, Vijay N; Dowdy, Steven F

Endosomal escape of RNA therapeutics: How do we solve this rate-limiting problem?

RNA疗法的内体逃逸:我们如何解决这一限速问题?

Dowdy, Steven F

DNA/RNA heteroduplex oligonucleotides: An unanticipated twist in the delivery of ASOs

DNA/RNA异源双链寡核苷酸:ASO递送中意想不到的转折

Setten, Ryan L; Dowdy, Steven F

Delivery of RNA Therapeutics: The Great Endosomal Escape!

RNA疗法的递送:伟大的内体逃逸!

Dowdy, Steven F; Setten, Ryan L; Cui, Xian-Shu; Jadhav, Satish G

The TAT Protein Transduction Domain as an Intra-Articular Drug Delivery Technology

TAT蛋白转导结构域作为一种关节内药物递送技术

Mailhiot, Sarah E; Thompson, Matthew A; Eguchi, Akiko E; Dinkel, Sabrina E; Lotz, Martin K; Dowdy, Steven F; June, Ronald K

Site Selective Antibody-Oligonucleotide Conjugation via Microbial Transglutaminase

利用微生物转谷氨酰胺酶进行位点选择性抗体-寡核苷酸偶联

Huggins, Ian J; Medina, Carlos A; Springer, Aaron D; van den Berg, Arjen; Jadhav, Satish; Cui, Xianshu; Dowdy, Steven F

Enhancing Endosomal Escape for Intracellular Delivery of Macromolecular Biologic Therapeutics.

增强内体逃逸以实现大分子生物治疗药物的细胞内递送

Lönn Peter, Kacsinta Apollo D, Cui Xian-Shu, Hamil Alexander S, Kaulich Manuel, Gogoi Khirud, Dowdy Steven F

Synthesis and Conjugation of Small Interfering Ribonucleic Neutral SiRNNs

小干扰核糖核中性SiRNN的合成与偶联

Hamil, Alexander S; Dowdy, Steven F

Combining CRISPR/Cas9 and rAAV Templates for Efficient Gene Editing

结合 CRISPR/Cas9 和 rAAV 模板实现高效基因编辑

Kaulich, Manuel; Dowdy, Steven F