Identification of small molecules that enhance aminoglycoside-mediated suppression of CFTR and NF1 nonsense mutations.
鉴定能增强氨基糖苷类药物对 CFTR 和 NF1 无义突变抑制作用的小分子。
期刊:Molecular Therapy Oncology
影响因子:5.3
doi:10.1016/j.omton.2026.201173
Sammons Joshua, Chen Jianguo, Thrasher Kari, Fu Lianwu, Du Ming, Wen Hui, Bostwick J Robert, Vinson Paige, Moukha-Chafiq Omar, Augelli-Szafran Corinne, Keeling Kim M, Wallis Deeann, Kesterson Robert A, Rowe Steven M, Bedwell David M