Treatment of monogenic and digenic dominant genetic hearing loss by CRISPR-Cas9 ribonucleoprotein delivery in vivo.
利用 CRISPR-Cas9 核糖核蛋白在体内递送治疗单基因和双基因显性遗传性听力损失
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-023-40476-7
Tao Yong, Lamas Veronica, Du Wan, Zhu Wenliang, Li Yiran, Whittaker Madelynn N, Zuris John A, Thompson David B, Rameshbabu Arun Prabhu, Shu Yilai, Gao Xue, Hu Johnny H, Pei Charles, Kong Wei-Jia, Liu Xuezhong, Wu Hao, Kleinstiver Benjamin P, Liu David R, Chen Zheng-Yi