日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models.

使用双AAV内含子载体的视网膜基因疗法治疗Stargardt病在大动物模型中安全有效

Ferla Rita, Pugni Eugenio, Lupo Mariangela, Tiberi Paola, Fioretto Federica, Perota Andrea, Duchi Roberto, Lagutina Irina, Gesualdo Carlo, Rossi Settimio, Ventrella Domenico, Elmi Alberto, McClinton Benjamin, Toomes Carmel, Xu Tongzhou, Molday Robert S, Surace Enrico M, Simonelli Francesca, Bacci Maria L, Galli Cesare, Memon Muhammad A, Shams Naveed, Auricchio Alberto, Trapani Ivana

Transabdominal ultrasound guided AAV9-GFP delivery in fetal pigs: a translational and minimally invasive model for in utero fetal gene therapy.

经腹部超声引导 AAV9-GFP 递送至胎猪:一种用于子宫内胎儿基因治疗的转化和微创模型。

Di Donfrancesco Alessia, Adelizzi Alessia, Giri Anastasia, Duchi Roberto, Boito Simona, Barandalla Maria, Massaro Giulia, Santanatoglia Chiara, Cappellozza Enrica, Perota Andrea, Di Meo Ivano, Tiranti Valeria, Bottani Emanuela, Galli Cesare, Persico Nicola, Brunetti Dario

Editorial: Tissue repair modeling of locomotor apparatus

社论:运动器官的组织修复建模

Cucchiarini, Magali; Dorey, Karel; Rey Rico, Ana; Duchi, Serena

Adherence to the Mediterranean Diet in Paediatric Patients with Inflammatory Bowel Disease and Functional Abdominal Pain Disorders-Comparative Study

儿童炎症性肠病和功能性腹痛患者坚持地中海饮食的比较研究

Ţincu, Iulia Florentina; Chenescu, Bianca Teodora; Duchi, Larisa Alexandra; Pleșca, Doina Anca

Controlled oxygen delivery to power tissue regeneration

控制氧气输送以促进组织再生

Zoneff, Elizabeth; Wang, Yi; Jackson, Colin; Smith, Oliver; Duchi, Serena; Onofrillo, Carmine; Farrugia, Brooke; Moulton, Simon E; Williams, Richard; Parish, Clare; Nisbet, David R; Caballero-Aguilar, Lilith M

Double transgenic neonatal porcine islets as an alternative source for beta cell replacement therapy.

双转基因新生猪胰岛作为β细胞替代疗法的替代来源

Mourad Nizar I, Perota Andrea, Xhema Daela, Duchi Roberto, Lagutina Irina, Galli Cesare, Gianello Pierre

NEST3D printed bone-mimicking scaffolds: assessment of the effect of geometrical design on stiffness and angiogenic potential

NEST3D 打印骨模拟支架:评估几何设计对刚度和血管生成潜力的影响

Stephanie E Doyle #, Micaela Pannella #, Carmine Onofrillo, Chiara Bellotti, Claudia Di Bella, Cathal D O'Connell, Elena Pirogova, Enrico Lucarelli, Serena Duchi

Changes in glial cell activation and extracellular vesicles production precede the onset of disease symptoms in transgenic hSOD1G93A pigs

转基因 hSOD1G93A 猪的神经胶质细胞活化和细胞外囊泡产生的变化先于疾病症状的出现

Maria Teresa Golia, Roberto Frigerio, Susanna Pucci, Francesca Sironi, Cassandra Margotta, Laura Pasetto, Camilla Testori, Elena Berrone, Francesco Ingravalle, Marcella Chiari, Alessandro Gori, Roberto Duchi, Andrea Perota, Luca Bergamaschi, Antonio D'Angelo, Giulia Cagnotti, Cesare Galli, Cristiano

Feasibility and barriers to rapid establishment of patient-derived primary osteosarcoma cell lines in clinical management

在临床管理中快速建立患者来源的原发性骨肉瘤细胞系的可行性及障碍

Chow, Thomas; Humble, William; Lucarelli, Enrico; Onofrillo, Carmine; Choong, Peter F; Di Bella, Claudia; Duchi, Serena

Characterization of a Romanian Pediatric Population with Eosinophilic Esophagitis

罗马尼亚嗜酸性食管炎患儿人群的特征分析

Tincu, Iulia Florentina; Bordei, Luiza Elena; Gales, Lucica Luminita; Duchi, Larisa Alexandra; Dobrescu, Loredana; Chenescu, Bianca Teodora